subject area of
- A new method for recombinant adeno-associated virus vector delivery to murine diaphragm. Academic Article
- Assessment of Cellular and Functional Biomarkers in Bivalves Exposed To Ecologically Relevant Abiotic Stressors Academic Article
- Clinical Outcomes After Long-Term Treatment With Alglucosidase Alfa in Infants and Children With Advanced Pompe Disease Academic Article
- Glycosylation-Independent Lysosomal Targeting of Acid Alpha-Glucosidase Enhances Muscle Glycogen Clearance in Pompe Mice Academic Article
- Impact of humoral immune response on distribution and efficacy of recombinant adeno-associated virus-derived acid alpha-glucosidase in a model of glycogen storage disease type II. Academic Article
- Metabolic and phenotypic characteristics of human skeletal muscle fibers as predictors of glycogen utilization during electrical stimulation. Academic Article
- Phylogenetic Analysis of Adp-Glucose Pyrophosphorylase Subunits Reveals a Role of Subunit Interfaces in the Allosteric Properties of the Enzyme Academic Article
- Physiological correction of Pompe disease by systemic delivery of adeno-associated virus serotype 1 vectors. Academic Article
- Pompe Disease Gene Therapy Academic Article
- Short- and Long-Term Response of Phytoplankton To Enso in Prydz Bay, Antarctica: Evidences From Field Measurements, Remote Sensing Data and Stratigraphic Biomarker Records Academic Article
- Spinal Delivery of Aav Vector Restores Enzyme Activity and Increases Ventilation in Pompe Mice Academic Article
- The Rna Binding Protein Csra Is a Pleiotropic Regulator of the Locus of Enterocyte Effacement Pathogenicity Island of Enteropathogenic Escherichia Coli Academic Article
- Unusual Histological Variant of Ewing's Sarcoma of Mandible Academic Article