subject area of
- A Combined Therapeutic Approach for Pyruvate Dehydrogenase Deficiency Using Self-Complementary Adeno-Associated Virus Serotype-Specific Vectors and Dichloroacetate Academic Article
- A Comprehensive Review of Retinal Gene Therapy Academic Article
- A Limited Innate Immune Response Is Induced By a Replication-Defective Herpes Simplex Virus Vector Following Delivery To the Murine Central Nervous System Academic Article
- A Simplified Immune Suppression Scheme Leads To Persistent Micro-Dystrophin Expression in Duchenne Muscular Dystrophy Dogs Academic Article
- A new method for recombinant adeno-associated virus vector delivery to murine diaphragm. Academic Article
- AAV-mediated gene therapy for retinal degeneration in the rd10 mouse containing a recessive PDEbeta mutation. Academic Article
- Aav Delivery of Wild-Type Rhodopsin Preserves Retinal Function in a Mouse Model of Autosomal Dominant Retinitis Pigmentosa Academic Article
- Aav Vector Biology in Primates: Finding the Missing Link? Academic Article
- Aav Vectors for Cardiac Gene Transfer: Experimental Tools and Clinical Opportunities Academic Article
- Aav-Based Rnai Silencing of Nadph Oxidase Gp91(Phox) Attenuates Cold-Induced Cardiovascular Dysfunction Academic Article
- Aav-Mediated Cone Rescue in a Naturally Occurring Mouse Model of Cnga3-Achromatopsia Academic Article
- Aav-Mediated Gene Therapy in the Guanylate Cyclase (Retgc1/Retgc2) Double Knockout Mouse Model of Leber Congenital Amaurosis Academic Article
- Aav6-Mediated Gene Silencing Fals Short Academic Article
- Ace2 and Ang-(1-7) Confer Protection Against Development of Diabetic Retinopathy Academic Article
- Achromatopsia as a Potential Candidate for Gene Therapy Academic Article
- Acoustic Accessibility Investigation for Ultrasound Mediated Treatment of Glycogen Storage Disease Type Ia Patients Academic Article
- Activation of the Nf-Kappa B Pathway By Adeno-Associated Virus (Aav) Vectors and Its Implications in Immune Response and Gene Therapy Academic Article
- Activity of Tar in Inducible Inhibition of Hiv Replication By Foamy Virus Vector Expressing Sirnas Under the Control of Hiv Ltr Academic Article
- Adeno Associated Viral Vector-Mediated Expression of Somatostatin in Rat Hippocampus Suppresses Seizure Development Academic Article
- Adeno-Associated Viral (Aav) Serotype 5 Vector Mediated Gene Delivery of Endothelin-Converting Enzyme Reduces a Beta Deposits in App+Ps1 Transgenic Mice Academic Article
- Adeno-Associated Virus Serotype 6 Capsid Tyrosine-To-Phenylalanine Mutations Improve Gene Transfer To Skeletal Muscle Academic Article
- Adeno-Associated Virus-Mediated Correction of a Canine Model of Glycogen Storage Disease Type Ia Academic Article
- Adeno-associated viral vectors and the retina. Academic Article
- Adeno-associated virus-based gene therapy for inherited disorders. Academic Article
- Adeno-associated virus-mediated expression of vascular endothelial growth factor peptides inhibits retinal neovascularization in a mouse model of oxygen-induced retinopathy. Academic Article
- Adeno-associated virus-mediated gene transfer for lung diseases. Academic Article
- Adipose Tissue-Derived Mesenchymal Stem Cell-Based Liver Gene Delivery Academic Article
- Alpha-1 Antitrypsin Protein and Gene Therapies Decrease Autoimmunity and Delay Arthritis Development in Mouse Model Academic Article
- An Inducible System for Highly Efficient Production of Recombinant Adeno-Associated Virus (Raav) Vectors in Insect Sf9 Cells Academic Article
- Angiotensin-converting enzyme 2 as a novel target for gene therapy for hypertension. Academic Article
- Animal Models of Hemophilia
- Arthritis Gene Therapy'S First Death Academic Article
- Biochemical Correction of Short-Chain Acyl-Coenzyme a Dehydrogenase Deficiency After Portal Vein Injection of Raav8-Scad Academic Article
- Calcium Upregulation By Percutaneous Administration of Gene Therapy in Cardiac Disease (Cupid Trial), a First-In-Human Phase 1/2 Clinical Trial Academic Article
- Calcium Upregulation By Percutaneous Administration of Gene Therapy in Cardiac Disease (Cupid) a Phase 2 Trial of Intracoronary Gene Therapy of Sarcoplasmic Reticulum Ca(2+)-Atpase in Patients With Advanced Heart Failure Academic Article
- Cancer-Induced Expansion and Activation of Cd11B(+)Gr-1(+) Cells Predispose Mice To Adenoviral-Triggered Anaphylactoid-Type Reactions Academic Article
- Cardiac Overexpression of Angiotensin Converting Enzyme 2 Protects the Heart From Ischemia-Induced Pathophysiology Academic Article
- Cardiovascular pharmacogenomics. Academic Article
- Caspase Inhibition With Xiap as An Adjunct To Aav Vector Gene-Replacement Therapy: Improving Efficacy and Prolonging the Treatment Window Academic Article
- Central Leptin Gene Therapy, a Substitute for Insulin Therapy To Ameliorate Hyperglycemia and Hyperphagia, and Promote Survival in Insulin-Deficient Diabetic Mice Academic Article
- Characterization of endotoxin and cationic liposome interaction. Academic Article
- Clinical Responses To Gene Therapy in Joints of Two Subjects With Rheumatoid Arthritis Academic Article
- Combination of Alpha-1 Antitrypsin and Doxycycline Suppresses Collagen-Induced Arthritis Academic Article
- Comparison of the Transduction Efficiency of Tyrosine-Mutant Adeno-Associated Virus Serotype Vectors in Kidney Academic Article
- Complex I Subunit Gene Therapy With Ndufa6 Ameliorates Neurodegeneration in Eae Academic Article
- Cone-Specific Expression Using a Human Red Opsin Promoter in Recombinant Aav Academic Article
- Correlation between DNA transfer and cystic fibrosis airway epithelial cell correction after recombinant adeno-associated virus serotype 2 gene therapy. Academic Article
- Current Strategies in the Management of Lysosomal Storage Diseases Academic Article
- Design of a Phase 1/2 Trial of Intracoronary Administration of Aav1/Serca2a in Patients With Heart Failure Academic Article
- Development of An Anti-Angiogenic Therapeutic Model Combining Scaav2-Delivered Sirnas and Noninvasive Photoacoustic Imaging of Tumor Vasculature Development Academic Article
- Differential Proteomics and Functional Research Following Gene Therapy in a Mouse Model of Leber Congenital Amaurosis Academic Article
- Differential Transduction Following Basal Ganglia Administration of Distinct Pseudotyped Aav Capsid Serotypes in Nonhuman Primates Academic Article
- Effect of Cntf On Retinal Ganglion Cell Survival in Experimental Glaucoma Academic Article
- Effect of Late-Stage Therapy On Disease Progression in Aav-Mediated Rescue of Photoreceptor Cells in the Retinoschisin-Deficient Mouse Academic Article
- Effects On Xiap Retinal Detachment-Induced Photoreceptor Apoptosis Academic Article
- Endogenous Il-10 Regulates Sepsis-Induced Thymic Apoptosis and Improves Survival in Septic Il-10 Null Mice Academic Article
- Engineered Aav Vector Minimizes in Vivo Targeting of Transduced Hepatocytes By Capsid-Specific Cd8(+) T Cells Academic Article
- Evaluation of Lateral Spread of Transgene Expression Following Subretinal Aav-Mediated Gene Delivery in Dogs Academic Article
- Ex vivo transduced liver progenitor cells as a platform for gene therapy in mice. Academic Article
- Experimental Cancer Therapy Using Restoration of Nad(+)-Linked 15-Hydroxyprostaglandin Dehydrogenase Expression Academic Article
- Fragile X Mental Retardation Protein Replacement Restores Hippocampal Synaptic Function in a Mouse Model of Fragile X Syndrome Academic Article
- Functional Rescue of P23H Rhodopsin Photoreceptors By Gene Delivery Academic Article
- Functional and Behavioral Restoration of Vision By Gene Therapy in the Guanylate Cyclase-1 (Gc1) Knockout Mouse Academic Article
- Gel-Mediated Delivery of Aav1 Vectors Corrects Ventilatory Function in Pompe Mice With Established Disease Academic Article
- Gene Delivery To Intestinal Epithelial Cells in Vitro and in Vivo With Recombinant Adeno-Associated Virus Types 1, 2 and 5 Academic Article
- Gene Delivery To Mitochondria By Targeting Modified Adenoassociated Virus Suppresses Leber'S Hereditary Optic Neuropathy in a Mouse Model Academic Article
- Gene Delivery of Wild-Type Rhodopsin Rescues Retinal Function in An Autosomal Dominant Retinitis Pigmentosa Mouse Model Academic Article
- Gene Therapy Approaches for Lysosomal Storage Disease: Next-Generation Treatment Academic Article
- Gene Therapy Prevents Photoreceptor Death and Preserves Retinal Function in a Bardet-Biedl Syndrome Mouse Model Academic Article
- Gene Therapy Rescues Cone Function in Congenital Achromatopsia Academic Article
- Gene Therapy Rescues Cone Structure and Function in the 3-Month-Old Rd12 Mouse: a Model for Midcourse Rpe65 Leber Congenital Amaurosis Academic Article
- Gene Therapy Rescues Photoreceptor Blindness in Dogs and Paves the Way for Treating Human X-Linked Retinitis Pigmentosa Academic Article
- Gene Therapy Using Adeno-Associated Virus Vectors Academic Article
- Gene Therapy Using Self-Complementary Y733F Capsid Mutant Aav2/8 Restores Vision in a Model of Early Onset Leber Congenital Amaurosis Academic Article
- Gene Therapy With Mitochondrial Heat Shock Protein 70 Suppresses Visual Loss and Optic Atrophy in Experimental Autoimmune Encephalomyelitis Academic Article
- Gene Therapy for Aromatic L-Amino Acid Decarboxylase Deficiency Academic Article
- Gene Therapy for Leber Congenital Amaurosis Caused By Rpe65 Mutations Safety and Efficacy in 15 Children and Adults Followed Up To 3 Years Academic Article
- Gene Therapy for Red-Green Colour Blindness in Adult Primates Academic Article
- Gene Therapy for Retinitis Pigmentosa Caused By Mfrp Mutations: Human Phenotype and Preliminary Proof of Concept Academic Article
- Gene Therapy of Gastric Cancer Using Light-Secreting Human Umbilical Cord Blood-Derived Mesenchymal Stem Cells Academic Article
- Gene Therapy of the Rheumatic Diseases: 1998 To 2008 Academic Article
- Gene therapy for autosomal dominant disorders of keratin. Academic Article
- Gene therapy for hypertension: sense and antisense strategies. Academic Article
- Gene therapy for mouse models of ADRP. Academic Article
- Gene therapy for obesity. Academic Article
- Gene therapy for treatment of inherited haematological disorders. Academic Article
- Gene therapy restores vision-dependent behavior as well as retinal structure and function in a mouse model of RPE65 Leber congenital amaurosis. Academic Article
- Gene-transfer technology: a preventive neurotherapy to curb obesity, ameliorate metabolic syndrome and extend life expectancy. Academic Article
- Generation of Novel Aav Variants By Directed Evolution for Improved Cftr Delivery To Human Ciliated Airway Epithelium Academic Article
- Genomic and Proteomic Approaches for Targeting of Angiotensin-Converting Enzyme2 for Cardiovascular Diseases Academic Article
- Getting Arthritis Gene Therapy Into the Clinic Academic Article
- Gitr Engagement Preferentially Enhances Proliferation of Functionally Competent Cd4(+)Cd25(+)Foxp3(+) Regulatory T Cells Academic Article
- Heart Failure-Inducible Gene Therapy Targeting Protein Phosphatase 1 Prevents Progressive Left Ventricular Remodeling Academic Article
- High-Efficiency Transduction and Correction of Murine Hemophilia B Using Aav2 Vectors Devoid of Multiple Surface-Exposed Tyrosines Academic Article
- High-Efficiency Transduction of Fibroblasts and Mesenchymal Stem Cells By Tyrosine-Mutant Aav2 Vectors for Their Potential Use in Cellular Therapy Academic Article
- Human Gene Therapy for Rpe65 Isomerase Deficiency Activates the Retinoid Cycle of Vision But With Slow Rod Kinetics Academic Article
- Human Retinal Gene Therapy for Leber Congenital Amaurosis Shows Advancing Retinal Degeneration Despite Enduring Visual Improvement Academic Article
- Human Rpe65 Gene Therapy for Leber Congenital Amaurosis: Persistence of Early Visual Improvements and Safety At 1 Year Academic Article
- Humoral and Cellular Capsid-Specific Immune Responses To Adeno-Associated Virus Type 1 in Randomized Healthy Donors Academic Article
- Hypothalamic Leptin Gene Therapy Prevents Weight Gain Without Long-Term Detrimental Effects On Bone in Growing and Skeletally Mature Female Rats Academic Article
- Hypothalamic rAAV-mediated GDNF gene delivery ameliorates age-related obesity. Academic Article
- Identification of Adeno-Associated Viral Vectors Suitable for Intestinal Gene Delivery and Modulation of Experimental Colitis Academic Article
- Immune responses to AAV capsid: are mice not humans after all? Academic Article
- Immune responses to recombinant adeno-associated virus vectors: putting preclinical findings into perspective. Academic Article
- Impact of humoral immune response on distribution and efficacy of recombinant adeno-associated virus-derived acid alpha-glucosidase in a model of glycogen storage disease type II. Academic Article
- Impact of the Underlying Mutation and the Route of Vector Administration On Immune Responses To Factor Ix in Gene Therapy for Hemophilia B Academic Article
- Improved Induction of Immune Tolerance To Factor Ix By Hepatic Aav-8 Gene Transfer Academic Article
- Improved Motor Performance in Dyt1 Delta Gag Heterozygous Knock-in Mice By Cerebellar Purkinje-Cell Specific Dyt1 Conditional Knocking-Out Academic Article
- Improvement and Decline in Vision With Gene Therapy in Childhood Blindness Academic Article
- In Vivo Anti-Tumor Effect of Expressing P14Arf-Tat Using a Fgf2-Targeted Cationic Lipid Vector Academic Article
- Indoleamine 2,3-Dioxygenase Attenuates Inhibitor Development in Gene-Therapy-Treated Hemophilia a Mice Academic Article
- Inhibition of P66Shca Redox Activity in Cardiac Muscle Cells Attenuates Hyperglycemia-Induced Oxidative Stress and Apoptosis Academic Article
- Innovative Vector Design: Cross-Packaged, Self-Complementary and Now Trans-Splicing Aav Vectors Academic Article
- Interferon alpha2b gene delivery using adenoviral vector causes inhibition of tumor growth in xenograft models from a variety of cancers. Academic Article
- Intra-Articular Gene Delivery and Expression of Interleukin-1Ra Mediated By Self-Complementary Adeno-Associated Virus Academic Article
- Lhon Gene Therapy Vector Prevents Visual Loss and Optic Neuropathy Induced By G11778a Mutant Mitochondrial Dna: Biodistribution and Toxicology Profile Academic Article
- Limb-Girdle Muscular Dystrophy Type 2D Gene Therapy Restores Alpha-Sarcoglycan and Associated Proteins Academic Article
- Long-Term Correction of Inhibitor-Prone Hemophilia B Dogs Treated With Liver-Directed Aav2-Mediated Factor Ix Gene Therapy Academic Article
- Long-Term Correction of Very Long-Chain Acyl-Coa Dehydrogenase Deficiency in Mice Using Aav9 Gene Therapy Academic Article
- Long-Term Preservation of Cone Photoreceptors and Restoration of Cone Function By Gene Therapy in the Guanylate Cyclase-1 Knockout (Gc1Ko) Mouse Academic Article
- Long-Term Rescue of Retinal Structure and Function By Rhodopsin Rna Replacement With a Single Adeno-Associated Viral Vector in P23H Rho Transgenic Mice Academic Article
- Long-Term Retinal Function and Structure Rescue Using Capsid Mutant Aav8 Vector in the Rd10 Mouse, a Model of Recessive Retinitis Pigmentosa Academic Article
- Long-Term Rna Interference Gene Therapy in a Dominant Retinitis Pigmentosa Mouse Model Academic Article
- Macrophage Migration Inhibitory Factor in the Nucleus of Solitary Tract Decreases Blood Pressure in Shrs Academic Article
- Management of Malignant Pleural Effusion By Suicide Gene Therapy in Advanced Stage Lung Cancer: a Case Series and Literature Review Academic Article
- Mathematical Modeling Predicts Synergistic Antitumor Effects of Combining a Macrophage-Based, Hypoxia-Targeted Gene Therapy With Chemotherapy Academic Article
- Molecular Anthropology Meets Genetic Medicine To Treat Blindness in the North African Jewish Population: Human Gene Therapy Initiated in Israel Academic Article
- N-Glycosylation Augmentation of the Cystic Fibrosis Epithelium Improves Pseudomonas Aeruginosa Clearance Academic Article
- NPY and cohorts in regulating appetite, obesity and metabolic syndrome: beneficial effects of gene therapy. Academic Article
- Near-Perfect Infectivity of Wild-Type Aav as Benchmark for Infectivity of Recombinant Aav Vectors Academic Article
- Next Generation of Adeno-Associated Virus 2 Vectors: Point Mutations in Tyrosines Lead To High-Efficiency Transduction At Lower Doses Academic Article
- Noninvasive monitoring of gene correction in dystrophic muscle. Academic Article
- Novel Anti-Vegf Chimeric Molecules Delivered By Aav Vectors for Inhibition of Retinal Neovascularization Academic Article
- Optimization of Continuous in Vivo Dopa Production and Studies On Ectopic Da Synthesis Using Raav5 Vectors in Parkinsonian Rats Academic Article
- Optimization of Recombinant Adeno-Associated Viral Vectors for Human Beta-Globin Gene Transfer and Transgene Expression Academic Article
- Orthopedic Gene Therapy in 2008 Academic Article
- Orthopedic Gene Therapyulost in Translation? Academic Article
- PKU is a reversible neurodegenerative process within the nigrostriatum that begins as early as 4 weeks of age in Pah(enu2) mice. Academic Article
- Partial Correction of the Cftr-Dependent Abpa Mouse Model With Recombinant Adeno-Associated Virus Gene Transfer of Truncated Cftr Gene Academic Article
- Peripheral Leptin Regulates Bone Formation Academic Article
- Peripheral targeting of the trigeminal ganglion via the infraorbital foramen as a therapeutic strategy. Academic Article
- Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized Aav Vector Academic Article
- Phase 2 Clinical Trial of a Recombinant Adeno-Associated Viral Vector Expressing Alpha(1)-Antitrypsin: Interim Results Academic Article
- Physiological correction of Pompe disease by systemic delivery of adeno-associated virus serotype 1 vectors. Academic Article
- Pivotal Role of Leptin-Hypothalamus Signaling in the Etiology of Diabetes Uncovered By Gene Therapy: a New Therapeutic Intervention? Academic Article
- Pompe Disease Gene Therapy Academic Article
- Positron Emission Tomography Imaging Demonstrates Correlation Between Behavioral Recovery and Correction of Dopamine Neurotransmission After Gene Therapy Academic Article
- Potential of gene therapy strategy for the treatment of hypertension. Academic Article
- Preclinical characterization of a recombinant adeno-associated virus type 1-pseudotyped vector demonstrates dose-dependent injection site inflammation and dissemination of vector genomes to distant sites. Academic Article
- Preservation of photoreceptor morphology and function in P23H rats using an allele independent ribozyme. Academic Article
- Pro-Opiomelanocortin Gene Transfer To the Nucleus of the Solitary Track But Not Arcuate Nucleus Ameliorates Chronic Diet-Induced Obesity Academic Article
- Progress and Prospects: Genetic Treatments for Disorders of Bones and Joints Academic Article
- Progress and Prospects: Immune Responses To Viral Vectors Academic Article
- Progress in direct striatal delivery of L-dopa via gene therapy for treatment of Parkinson's disease using recombinant adeno-associated viral vectors. Academic Article
- Prolonged recovery of retinal structure/function after gene therapy in an Rs1h-deficient mouse model of x-linked juvenile retinoschisis. Academic Article
- Prophylactic Immune Tolerance Induced By Changing the Ratio of Antigen-Specific Effector To Regulatory T Cells Academic Article
- Prospects for Retinal Cone-Targeted Gene Therapy Academic Article
- Raav2/5 Gene-Targeting To Rods: Dose-Dependent Efficiency and Complications Associated With Different Promoters Academic Article
- Recombinant Adeno-Asociated Virus-Mediated Global Anterograde Delivery of Glial Cell Line-Derived Neurotrophic Factor To the Spinal Cord: Comparison of Rubrospinal and Corticospinal Tracts in the Rat Academic Article
- Recombinant Adeno-Associated Viral Vector Reference Standards
- Recombinant Adeno-Associated Virus-Mediated Gene Transfer for the Potential Therapy of Adenosine Deaminase-Deficient Severe Combined Immune Deficiency Academic Article
- Recombinant adeno-associated viral vector-mediated glial cell line-derived neurotrophic factor gene transfer protects nigral dopamine neurons after onset of progressive degeneration in a rat model of Parkinson's disease. Academic Article
- Recombinant adeno-associated viral vectors as therapeutic agents to treat neurological disorders. Academic Article
- Recombinant adeno-associated viral vectors in the nervous system. Academic Article
- Reduction in Severity of a Herpes Simplex Virus Type 1 Murine Infection By Treatment With a Ribozyme Targeting the U(L)20 Gene Rna Academic Article
- Regenerative Medicine for the Special Senses: Restoring the Inputs Academic Article
- Regression of Schwannomas Induced By Adeno-Associated Virus-Mediated Delivery of Caspase-1 Academic Article
- Regulated Protein Expression for in Vivo Gene Therapy for Neurological Disorders: Progress, Strategies, and Issues Academic Article
- Restoration of Vision in the Pde6 Beta-Deficient Dog, a Large Animal Model of Rod-Cone Dystrophy Academic Article
- Retinal Gene Therapy With a Large Myo7a Cdna Using Adeno-Associated Virus Academic Article
- Retrograde Gene Delivery To Hypoglossal Motoneurons Using Adeno-Associated Virus Serotype 9 Academic Article
- Ribozyme gene therapy for autosomal dominant retinal disease. Academic Article
- Rnai Inhibition of Mineralocorticoid Receptors Prevents the Development of Cold-Induced Hypertension Academic Article
- Role of Molecular Genetics in Hemophilia: From Diagnosis To Therapy Academic Article
- Self-complementary AAV-mediated gene therapy restores cone function and prevents cone degeneration in two models of Rpe65 deficiency. Academic Article
- Signs of Progress in Gene Therapy for Muscular Dystrophy Also Warrant Caution Academic Article
- Soluble Flt-1 Gene Therapy Ameliorates Albuminuria But Accelerates Tubulointerstitial Injury in Diabetic Mice Academic Article
- Spinal Delivery of Aav Vector Restores Enzyme Activity and Increases Ventilation in Pompe Mice Academic Article
- Stable Integration of Recombinant Adeno-Associated Virus Vector Genomes After Transduction of Murine Hematopoietic Stem Cells Academic Article
- Stem cell therapy for inherited metabolic disorders of the liver. Academic Article
- Strategies for Improving the Transduction Efficiency of Single-Stranded Adeno-Associated Virus Vectors in Vitro and in Vivo Academic Article
- Striatal Pleiotrophin Overexpression Provides Functional and Morphological Neuroprotection in the 6-Hydroxydopamine Model Academic Article
- Suppression of Rds Expression By Sirna and Gene Replacement Strategies for Gene Therapy Using Raav Vector Academic Article
- Sustained Alpha-Sarcoglycan Gene Expression After Gene Transfer in Limb-Girdle Muscular Dystrophy, Type 2D Academic Article
- Sustained Transgene Expression Despite T Lymphocyte Responses in a Clinical Trial of Raav1-Aat Gene Therapy Academic Article
- Synergy Between Leptin Therapy and a Seemingly Negligible Amount of Voluntary Wheel Running Prevents Progression of Dietary Obesity in Leptin-Resistant Rats Academic Article
- Targeted Decorin Gene Therapy Delivered With Adeno-Associated Virus Effectively Retards Corneal Neovascularization in Vivo Academic Article
- Targeting Gene Expression To Cones With Human Cone Opsin Promoters in Recombinant Aav Academic Article
- The Aav9 Receptor and Its Modification To Improve in Vivo Lung Gene Transfer in Mice Academic Article
- The Angiotensin-Converting Enzyme 2/Angiogenesis-(1-7)/Mas Axis Confers Cardiopulmonary Protection Against Lung Fibrosis and Pulmonary Hypertension Academic Article
- The Genome of Self-Complementary Adeno-Associated Viral Vectors Increases Toll-Like Receptor 9-Dependent Innate Immune Responses in the Liver Academic Article
- The Human Rhodopsin Kinase Promoter in An Aav5 Vector Confers Rod- and Cone-Specific Expression in the Primate Retina Academic Article
- The Promise of Cell-Based Therapies for Diabetic Complications Challenges and Solutions Academic Article
- The Pros and Cons of Immunomodulatory Il-10 Gene Therapy With Recombinant Aav in a Cftr(-/-)-Dependent Allergy Mouse Model Academic Article
- The Threefold Protrusions of Adeno-Associated Virus Type 8 Are Involved in Cell Surface Targeting as Well as Postattachment Processing Academic Article
- The effects of rAAV2-mediated NGF gene delivery in adult and aged rats. Academic Article
- Therapeutic Efficacy of Bone Marrow Transplant, Intracranial Aav-Mediated Gene Therapy, Or Both in the Mouse Model of Mps Iiib Academic Article
- Tlr3 Signaling Does Not Affect Organ-Specific Immune Responses To Factor Ix in Aav Gene Therapy Academic Article
- Tnf-Alpha Expression in the Ucb-Mscs as Stable Source Inhibits Gastric Cancers Growth in Nude Mice Academic Article
- To subjugate NPY is to improve the quality of life and live longer. Academic Article
- Towards a Raav-Based Gene Therapy for Ada-Scid: From Ada Deficiency To Current and Future Treatment Strategies Academic Article
- Transgene persistence and cell turnover in the diarthrodial joint: implications for gene therapy of chronic joint diseases. Academic Article
- Transient B Cell Depletion Or Improved Transgene Expression By Codon Optimization Promote Tolerance To Factor Viii in Gene Therapy Academic Article
- Translating the Genomics Revolution: the Need for An International Gene Therapy Consortium for Monogenic Diseases Academic Article
- Treatment of Leber Congenital Amaurosis Due To Rpe65 Mutations By Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector: Short-Term Results of a Phase I Trial Academic Article
- Treatment of Nonhealing Diabetic Foot Ulcers With a Platelet-Derived Growth Factor Gene-Activated Matrix (Gam501): Results of a Phase 1/2 Trial Academic Article
- Triple Combination of Sirnas Targeting Tgf Beta 1, Tgf Beta R2, and Ctgf Enhances Reduction of Collagen I and Smooth Muscle Actin in Corneal Fibroblasts Academic Article
- Tyrosine-Mutant Aav8 Delivery of Human Mertk Provides Long-Term Retinal Preservation in Rcs Rats Academic Article
- Versatile Somatic Gene Transfer for Modeling Neurodegenerative Diseases Academic Article
- Viral Vectors for in Vivo Gene Transfer in Parkinson'S Disease: Properties and Clinical Grade Production Academic Article
- Vision 1 Year After Gene Therapy for Leber's Congenital Amaurosis Academic Article
- Xiap Therapy Increases Survival of Transplanted Rod Precursors in a Degenerating Host Retina Academic Article